The Trump administration announced a new FDA approval pathway for individualized gene editing for rare diseases.
The FDA has introduced a new approval process for targeted individualized therapies, including genome editing and RNA-based ...
Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders ...
Despite widespread misconceptions, eating disorders aren’t a choice, they’re serious, potentially life-threatening conditions. While social and environmental factors do influence someone’s risk of ...
Psychiatric disorders can share common genetic influences, which means parts of DNA can be at the root of more than one mental condition, new research has found. The study, led by researchers at Texas ...
St. Louis Families Unite for Rare Disease Day 2026 as Take Part Foundation Advances Critical Genetic Testing and ...
"It's a slow-moving train wreck," Mike Graglia says about his 12-year-old son Tony's rare genetic disease with no cure. Caused by a tiny fluke of nature—a mutation in a gene known as a SYNGAP1—the non ...
A rare inherited neurodevelopmental disorder has been officially named after an Abu Dhabi-based geneticist at Burjeel Medical ...
New research uncovers how cannabis addiction, not casual use, is genetically tied to severe mental health conditions, raising red flags for policy, treatment, and prevention. Study: The genetic ...